Researcher develops, proves effectiveness of new drug for spinal muscular atrophy

15 septiembre 2014

Approximately one out of every 40 individuals in the United States is a carrier of the gene responsible for spinal muscular atrophy (SMA), According to recent studies. This illness is a neurodegenerative disease that causes muscles to weaken over time. Now, researchers have made a recent breakthrough with the development of a new compound found to be highly effective in animal models of the disease.